RNA-Targeting Strategy to Repair Genetic Cause of ALS and Frontotemporal Dementia
A novel compound eliminates disease-causing segments of RNA associated with ALS and dementia, and restores the health of neurons in mouse models
#Neuroscience #Neurology #NeurodegenerativeDiseases #ALS #FTD #Dementia
#Genetics #GeneticDiseases #RareDiseases
#MolecularTherapy #ToxicRNA #RNAtargeting
#Biomedicine